First treatment for Alexander disease.
1 report so far. New developments are added to this thread as they happen.
- Sep 3, 2026FDA APPROVES FIRST-EVER DRUG FOR THE DISORDERFDA approval · 54 patients
FDA approves first drug for Alexander disease, a rare brain disorder
A spinal injection given every three months is now the first approved treatment aimed at the cause of Alexander disease, a genetic brain disorder that affects fewer than one in a million people.