Gene therapy for an inherited swallowing disorder.
1 report so far. New developments are added to this thread as they happen.
- Oct 28, 2026EARLY RESULTS: EVERY TREATED PATIENT RESPONDEDCompany results · 9 people
Gene therapy improved swallowing in all 9 patients so far, maker says
Benitec says every person treated with its one-time gene therapy for an inherited muscle disease that weakens swallowing met its response goals. The study is small and has no comparison group.