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One-time gene therapy for Dravet syndrome.

1 report so far. New developments are added to this thread as they happen.

  1. Oct 30, 2026
    EARLY RESULTS IN 21 CHILDRENEarly trials · 21 children

    One-time gene therapy for severe child epilepsy cut seizures, maker says

    Encoded Therapeutics says 21 young children with Dravet syndrome had fewer seizures and gained skills after a single gene therapy injection. The early studies had no comparison group.