One-time gene therapy for Dravet syndrome.
1 report so far. New developments are added to this thread as they happen.
- Oct 30, 2026EARLY RESULTS IN 21 CHILDRENEarly trials · 21 children
One-time gene therapy for severe child epilepsy cut seizures, maker says
Encoded Therapeutics says 21 young children with Dravet syndrome had fewer seizures and gained skills after a single gene therapy injection. The early studies had no comparison group.