Gene correction for sickle cell disease from Kamau.
1 report so far. New developments are added to this thread as they happen.
- Nov 4, 20263 PATIENTS OFF TRANSFUSIONS AFTER MUTATION FIXEDCompany results · 3 people
Gene fix for sickle cell freed 3 patients from transfusions, maker says
Kamau Therapeutics says rewriting the single faulty DNA letter behind sickle cell disease restored normal adult blood protein in three patients, none of whom have had pain crises since.