Gene editing inside the body for Wilson's disease.
1 report so far. New developments are added to this thread as they happen.
- Oct 5, 2026FIRST PATIENT TREATED IN FIRST HUMAN TRIALTrial underway · no data yet
First patient gets a one-time gene fix for Wilson's disease, maker says
Prime Medicine says the first person has received a one-time infusion that aims to repair the gene behind Wilson's disease, a rare illness that lets copper build up in the body.